Research record changes

The latest 100 trial status and retraction changes detected since change tracking began. Dates show when RareWays recorded the change, which may be later than the source update. Earlier history is unavailable.

1. A Real-World Medical Chart Review of Spinal Muscular Atrophy Patients Treated With Onasemnogene Abeparvovec in Saudi Arabia

   RECRUITING → NOT YET RECRUITING

   Recorded 2026-10-14

   View record

2. Self-Efficacy Enhancement Among Online Support Group of Primary Caregivers of Children With Neuro Muscular Dystrophy

   NOT YET RECRUITING → ACTIVE NOT RECRUITING

   Recorded 2026-10-09

   View record

3. Real World Clinical Effectiveness & Safety of Vesemnogene Lantuparvovec for Spinal Muscular Atrophy (SMA) in Low-middle Income Countries (LMIC).

   RECRUITING → WITHDRAWN

   Recorded 2026-10-01

   View record

4. Ultrasonographic Muscle Assessment and Functional Scales in Spinal Muscular Atrophy

   ACTIVE NOT RECRUITING → UNKNOWN

   Recorded 2026-10-01

   View record

5. Outcome Measures and Biomarkers in a Cohort of Spinal Muscular Atrophy Type III/ IV Patients

   ACTIVE NOT RECRUITING → UNKNOWN

   Recorded 2026-10-01

   View record

6. Outpatient Rehabilitation Intervention for Young Children With SMA

   RECRUITING → UNKNOWN

   Recorded 2026-10-01

   View record

7. MAP THE SMA: a Machine-learning Based Algorithm to Predict THErapeutic Response in Spinal Muscular Atrophy

   RECRUITING → UNKNOWN

   Recorded 2026-10-01

   View record

8. Spinal Muscular Atrophy Neonatal Screening Program

   RECRUITING → UNKNOWN

   Recorded 2026-10-01

   View record

9. Risdiplam in Patients With Spinal Muscular Atrophy Previously Treated With Nusinersen

   ACTIVE NOT RECRUITING → UNKNOWN

   Recorded 2026-10-01

   View record

10. Clinical Trial to Assess the Safety and Efficacy of EXG001-307 in Patients with Spinal Muscular Atrophy Type 1

    ENROLLING BY INVITATION → UNKNOWN

    Recorded 2026-10-01

    View record

11. A Review of the Management and Outcomes of Children With SMA in the West Midlands During 2017-2022

    RECRUITING → UNKNOWN

    Recorded 2026-10-01

    View record

12. Holter of Movement in Patients with SMA Undergoing Treatment.

    ACTIVE NOT RECRUITING → UNKNOWN

    Recorded 2026-10-01

    View record

13. Longitudinal Data Collection in Pediatric and Adult Patients With Spinal Muscular Atrophy in Latin America

    ACTIVE NOT RECRUITING → UNKNOWN

    Recorded 2026-10-01

    View record

14. High-intensity Interval Training in Patients With Spinal Muscular Atrophy

    RECRUITING → UNKNOWN

    Recorded 2026-10-01

    View record

15. Assessing the Fertility Status of Men With Spinal Muscular Atrophy (SMA)

    RECRUITING → UNKNOWN

    Recorded 2026-10-01

    View record

16. Gut Peptides and Bone Remodeling in Children With Neuromuscular Disorders

    RECRUITING → TERMINATED

    Recorded 2026-10-01

    View record