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Research record changes

The latest 100 trial status and retraction changes detected since change tracking began. Dates show when RareWays recorded the change, which may be later than the source update. Earlier history is unavailable.

  1. An Open Label Dose Escalation Study to Assess the Safety, Tolerability, and Pharmacologic Properties of High Dose Ambroxol Hydrochloride in Adult (≥ 18 Years of Age) Subjects With MPS III

    RECRUITING → UNKNOWN

    Recorded 2026-10-01

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  2. The Natural History Study of Patients With Sanfilippo Disease(s) (MPS3)

    RECRUITING → UNKNOWN

    Recorded 2026-10-01

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  3. An Open-label Phase I/II Study of JR-446 in Mucopolysaccharidosis Type IIIB

    RECRUITING → ACTIVE NOT RECRUITING

    Recorded 2026-10-01

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