Research record changes

The latest 100 trial status and retraction changes detected since change tracking began. Dates show when RareWays recorded the change, which may be later than the source update. Earlier history is unavailable.

1. A Study to Evaluate the Safety and Efficacy of Nizubaglustat (AZ-3102) in Patients With GM2 Gangliosidosis or Niemann-Pick Type C Disease

   RECRUITING → ACTIVE NOT RECRUITING

   Recorded 2026-10-14

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2. Phase 3 Study to Evaluate Intravenous Trappsol(R) Cyclo(TM) in Pediatric and Adult Patients With Niemann-Pick Disease Type C1

   ACTIVE NOT RECRUITING → UNKNOWN

   Recorded 2026-10-01

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