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Coverage: 2020-01-01 onwards, with up to 300 results per query from PubMed and Europe PMC and separate limits on other sources. This is a selected index, not a complete literature search.
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Dravet Syndrome: Research Summary
Printed from RareWays (rareways.org)
For general awareness only. Not medical advice. Discuss all care options with your healthcare team.
5 Most Recent Research Articles
- 1.
Clinical and Therapeutic Profile of Dravet Syndrome in Patients Followed at a Brazilian Pediatric Referral Center: Real-World Data from a Tertiary Service
Lisandra Coneglian Farias Rigoldi et al., Journal of Clinical Medicine (16 October 2026)
https://doi.org/10.3390/jcm15208034
- 2.
SCN1A haploinsufficiency disrupts neural progenitor networks and accelerates neurogenesis in human Dravet syndrome forebrain assembloids
Deepika Dogra et al., bioRxiv (Cold Spring Harbor Laboratory) (16 October 2026)
https://doi.org/10.64898/2026.10.14.758626
- 3.
SCN1A-Related Epilepsies: Clinical Spectrum and Mechanisms
Ja-Un Moon et al., Current Issues in Molecular Biology (2 October 2026)
https://doi.org/10.3390/cimb48101023
- 4.
Getting the diagnosis right in adults with childhood-onset epileptic encephalopathies: Lennox-Gastaut and Dravet syndromes-lessons from clinical practice
Lucia Šmahovská et al., Neurologie pro praxi (2 October 2026)
https://doi.org/10.36290/neu.2026.055
- 5.
Efficacy of Dravet Syndrome Treatments in a Subset of Individuals with 2q24.3 Deletion: A-5 Patient Case Series.
Kashima Daniel T et al., Journal of child neurology (1 October 2026)
https://pubmed.ncbi.nlm.nih.gov/41564166/
Clinical Trials : Currently Recruiting (Australia)
Ask your doctor whether you or your child may be eligible for any of these trials. Each has its ID and full eligibility criteria at the link shown.
- 1.
BMB-101 in Absence Epilepsy and DEE
NCT06401538 · Recruiting · Phase 2 · Bright Minds Biosciences Pty Ltd
Ages 18 to 65
https://clinicaltrials.gov/study/NCT06401538
- 2.
A Clinical Study to Evaluate the Safety and Efficacy of ETX101 in Infants and Children With SCN1A-Positive Dravet Syndrome
NCT05419492 · Recruiting · Phase 1 / Phase 2 · Encoded Therapeutics
Ages 6 Months to 17
https://clinicaltrials.gov/study/NCT05419492
Source: RareWays research directory. Data from PubMed, Europe PMC, OpenAlex, ClinicalTrials.gov.
Always verify information with your healthcare team before making any decisions about your care.
Dravet Syndrome
Dravet syndrome is a rare, severe form of epilepsy that begins in the first year of life, often with seizures triggered by fever. Children may later develop other seizure types, delays in development and problems with movement and behaviour. It is most often caused by a change in the SCN1A gene. Management focuses on seizure control with specific medicines, avoiding triggers and supportive care.
This overview is general information, not an individual medical assessment. Research is selected automatically and may include mismatches. How we select and explain research.
Most Recent Research
Background: Dravet syndrome (DS) is a severe developmental and epileptic encephalopathy, and data from low- and middle-income countries remain scarce. We characterized the clinical, genetic, and therapeutic profiles of patients with DS at a Brazilian tertiary referral center. Methods: This retrospective cross-sectional study included 27 patients with clinically and genetically confirmed DS (pathogenic/likely pathogenic SCN1A variants). Outcomes were ≥6-month and ≥12-month seizure freedom and seizure control in the previous month, described by treatment exposure without inferential testing. Results: The median age at seizure onset was 4 months and at diagnosis 42 months; the median individual onset-to-diagnosis interval was 29 months (range, 4–283; n = 14). All patients received polytherapy; 51.9% used cannabidiol, 40.7% vagus nerve stimulation, and 7.4% fenfluramine. Only 2/20 patients (10.0%) achieved ≥6-month and 1/20 (5.0%) ≥ 12-month seizure freedom. All six patients seizure-free in the previous month were receiving valproate, a descriptive finding likely reflecting confounding by indication. Recorded comorbidities, mainly autism spectrum disorder (29.6%), were likely underestimated in the absence of systematic neurodevelopmental assessment. Conclusions: This Brazilian DS cohort showed marked diagnostic delay, high seizure burden, and limited access to DS-specific therapies. These findings support earlier genetic testing and broader access to recommended treatments and generate hypotheses for larger prospective studies.
Common Questions
What is Dravet Syndrome?
Dravet syndrome is a rare, severe form of epilepsy that begins in the first year of life, often with seizures triggered by fever. Children may later develop other seizure types, delays in development and problems with movement and behaviour. It is most often caused by a change in the SCN1A gene. Management focuses on seizure control with specific medicines, avoiding triggers and supportive care.
How many clinical trials are available for Dravet Syndrome?
RareWays currently indexes 57 clinical trials for Dravet Syndrome, of which 9 are actively recruiting. These counts cover indexed trials across countries, not just your country. An Australian site does not necessarily mean that site is recruiting. Check locations, eligibility and current availability with the study team.
Where does the research data for Dravet Syndrome come from?
RareWays aggregates research from PubMed, Europe PMC, OpenAlex, and ClinicalTrials.gov. Data is refreshed automatically every day. All articles and trials link directly to their original sources.
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